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Targeted replacement of full-length CFTR in human airway stem cells by CRISPR-Cas9 for pan-mutation correction in the endogenous locus
Sriram Vaidyanathan
, Ron Baik
,
Lu Chen
, Dawn T. Bravo
, Carlos J. Suarez
, Shayda M. Abazari
, Ameen A. Salahudeen
, Amanda M. Dudek
, Christopher A. Teran
, Timothy H. Davis
, Ciaran M. Lee
, Gang Bao
, Scott H. Randell
, Steven E. Artandi
, Jeffrey J. Wine
, Calvin J. Kuo
, Tushar J. Desai
, Jayakar V. Nayak
, Zachary M. Sellers
, Matthew H. Porteus
Nuclear Dynamics and Cancer (NDC)
Greenberg Pancreatic Cancer Institute
Stanford University
Department of Otolaryngology–Head and Neck Surgery
Rice University
University of North Carolina at Chapel Hill
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