Long-term functional correction of cystathionine β-synthase deficiency in mice by adeno-associated viral gene therapy

Warren D. Kruger, Hyung-Ok Lee, Christiana O. Salami, Stephen M. Kaminsky, Ronald G. Crystal

Research output: Contribution to journalArticlepeer-review

11 Scopus citations

Search results

  • Laboratory Animal Facility

    Patterson, MLAS, CMAR, RLATg, ILAM, K. S. (Director), Pimble, AS, A. T. (Manager) & Tuohy VMD, K. (Staff)

    Equipment/facility: Facility