Long-term functional correction of cystathionine β-synthase deficiency in mice by adeno-associated viral gene therapy

  • Warren D. Kruger
  • , Hyung-Ok Lee
  • , Christiana O. Salami
  • , Stephen M. Kaminsky
  • , Ronald G. Crystal

Research output: Contribution to journalArticlepeer-review

16 Scopus citations

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  • Laboratory Animal Facility

    Patterson, MLAS, CMAR, RLATg, ILAM, K. S. (Director), Pimble, AS, A. T. (Manager) & Tuohy VMD, K. (Staff)

    Equipment/facility: Facility